delandistrogene moxeparvovec

1 Drug classified under this active ingredient

Gene Therapy. delandistrogene moxeparvovec 1.33 X 10^13.
Vial. Sol. for inf. 1.33 x 10¹³ vector genomes/ml  10-70 vials X 10 ml
For single-dose IV infusion only. Recommended dose is 1.33 × 10¹⁴ vector genomes per kilogram (vg/kg) of BW (or 10 mL/kg BW) for pts weighing less than 70 kg or 9.31 × 10¹⁵ vg total fixed dose for pts weighing 70 kg or greater. See full prescription info.
Tmt. of ambulatory ped. pts aged 4 to under 8 years with Duchenne musc. dystrophy (DMD) with a confirmed mutation in the DMD gene.
C/I: Hypersens. Any deletion in exon 8 and/or exon 9, including a deletion of any portion or the entirety of these exons, in the DMD gene.