eladocagene exuparvovec

1 Drug classified under this active ingredient

Gene Therapy. eladocagene exuparvovec 5.6 X10^11 vg/ml.
Solution for infusion 1X 0.5 ml
 1.8 × 10¹¹ vg delivered as four 0.08 mL (0.45 × 10¹¹ vg) infusions ( 2 per putamen)
Tmt. of pts aged 18 months and older with a clinical, molecular, and genetically confirmed diagnosis of aromatic L-amino acid decarboxylase (AADC) defic. with a sev. phenotype.
C/I:  hypersens.